Skeletal dysplasia are a group of conditions caused by abnormalities in the development, growth or maintenance of the human skeleton. Many of these conditions have had their molecular basis revealed over the past 20 years and, recently, several potential precision therapies have emerged for these conditions.
This talk will overview new emerging therapies for achondroplasia and Schmid metaphyseal dysplasia as examples of this new paradigm, and discuss the clinical trials that are evaluating the safety and effectiveness of these new treatments.
Lobby
Video on Demand
Exhibition Halls
Poster Gallery
PROGRAMME